#rare disease
articles
Health
Ladders to Cures Bets on 'Nodal Biology' to Make Rare Disease Drugs Profitable
A Harvard-led accelerator is hunting for shared biological mechanisms across rare diseases, aiming to build single drugs...
Health
CureDuchenne's New Campaign Uses Birthday Parties to Urgency Around Fatal Genetic Disease
The 'A Cure Can't Wait' push, created pro bono by Horizon Media, reframes children's birthdays as a stark reminder that ...